Danon Disease Clinical Trials

8 clinical trials for Danon Disease across international registries, including 4 currently recruiting participants. Compare status, phase, eligibility criteria and locations.

• Danon Disease Natural History Study — RECRUITING
• A Gene Therapy Study of RP-A501 in Male Patients With Danon Disease — RECRUITING · PHASE2
• Precision Diagnosis and Risk Stratification of Rare Cardiomyopathies Based on Novel Cardiac Magnetic Resonance Techniques — RECRUITING
• Rare Glycogen Storage Diseases Natural History Study — RECRUITING
• Gene Therapy for Danon Disease: A Phase 2 Study Evaluating the Efficacy and Safety of Intravenously Administered Adeno-Associated Virus Serotype 9 (rAAV9) Vector Containing the Human LAMP2 Isoform B Transgene (RP-A501; AAV9.LAMP2B) in Male Patients with Danon Disease — TERMINATED · PHASE2
• Natural History of Danon Disease — COMPLETED
• Gene Therapy for Male Patients With Danon Disease (DD) Using RP-A501; AAV9.LAMP2B — OTHER · PHASE1
• The Natural History of Danon Disease — OTHER

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