Duchenne Muscular Dystrophy Clinical Trials

443 clinical trials for Duchenne Muscular Dystrophy across international registries, including 89 currently recruiting participants. Compare status, phase, eligibility criteria and locations.

• Phase 2 Study of SAT-3247 in Pediatric Ambulatory Patients — RECRUITING · PHASE2
• Once Weekly Infant Corticosteroid Trial for DMD — RECRUITING · PHASE4
• A Study in Participants With Duchenne Muscular Dystrophy Amenable to Exon 44 Skipping to Evaluate the Safety and Efficacy of ENTR-601-44 — RECRUITING · PHASE1
• A Study in Participants With Duchenne Muscular Dystrophy Amenable to Exon 45 Skipping to Evaluate the Safety and Efficacy of ENTR-601-45 — RECRUITING · PHASE1
• A Study of SGT-003 Gene Therapy in Ambulant Males With Duchenne Muscular Dystrophy (IMPACT DUCHENNE) — RECRUITING · PHASE3
• A Study to Investigate the Safety and Biodistribution of a Single Intrathecal (IT) Injection of INS1201 in Ambulatory Males With Duchenne Muscular Dystrophy (DMD) — RECRUITING · PHASE1
• Modeling Mortality in Duchenne Muscular Dystrophy Cardiomyopathy: Identification of Surrogate Outcome Measures for DMD Drug Trials — RECRUITING
• Efficacy, Safety and Tolerability of Givinostat in Non-ambulant Patients With Duchenne Muscular Dystrophy — RECRUITING · PHASE3
• An Open-Label Extension Study to Evaluate the Long-term Safety and Efficacy of BMN 351 in Participants With Duchenne Muscular Dystrophy — RECRUITING · PHASE2
• Sodium/Glucose Cotransporter-2 Inhibitors (SGLT2i) Therapy in Duchenne Cardiomyopathy — RECRUITING · PHASE1
• Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy-SUMMIT — RECRUITING
• Parent and Infant Inter(X)Action Intervention (PIXI) — RECRUITING · NA
• A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE) — RECRUITING · PHASE1
• A Study to Evaluate the Tolerability, Safety and Efficacy of GNR-097 Gene Therapy in Pediatric Patients With Duchenne Muscular Dystrophy — RECRUITING · PHASE1
• A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) - Non-Ambulatory Cohort — RECRUITING · PHASE1
• A Phase 2, Open-Label Long-Term Extension Study in Participants With Duchenne Muscular Dystrophy Amenable to Exon Skipping to Assess the Long-Term Safety, Tolerability, Pharmacokinetics, and Efficacy of Endosomal Escape Vehicle Phosphorodiamidate Morpholino Oligomer Platform Products (ELEVATE-LTE) — RECRUITING · PHASE2
• A Remote Study Using Technology to Assess Outcomes in DMD — RECRUITING
• Efficacy, Safety, and Tolerability of Zeleciment Rostudirsen (DYNE-251) Administered Intravenously Every 4 Weeks in Ambulatory Participants With Duchenne Muscular Dystrophy (FORZETTO) — RECRUITING · PHASE3
• Duchenne Electronic Health Record Study — RECRUITING
• A Phase 3, Randomized, Double-Blind, Placebo-Controlled, Global Study with an Open-Label Extension to Evaluate the Efficacy and Safety of Intravenous AOC 1044 (delpacibart zotadirsen) for the Treatment of DMD with Gene Mutations Amenable to Exon 44 Skipping — RECRUITING · PHASE3
• Wearable Technology to Evaluate Hyperglycemia and HRV in DMD — RECRUITING
• The Effect of Virtual Reality Applications on Upper Extremity Functions in Patients With Duchenne Muscular Dystrophy — RECRUITING · NA
• Vasodilator and Exercise Study for DMD (VASO-REx) — RECRUITING · PHASE2
• The Duchenne Registry — RECRUITING
• Safety and Dystrophin Expression of SPOT-03 in Duchenne Muscular Dystrophy (DMD) Patients — RECRUITING · PHASE1
• An Observational Study Comparing Delandistrogene Moxeparvovec (ELEVIDYS) With Standard of Care in Participants With Duchenne Muscular Dystrophy — RECRUITING
• The Baby Duchenne Study: Characterizing Developmental and Clinical Outcomes in the First Three Years in Children With Duchenne Muscular Dystrophy — RECRUITING
• Usability and User Experience of a Virtual Reality Rehabilitation Game Platform in Individuals With Duchenne Muscular Dystrophy — RECRUITING
• Real-time magnetic resonance imaging (RT-MRI) for evaluating changes in swallowing, reflux, and lung mechanics in children with spinal muscular atrophy or Duchenne muscular dystrophy before and after spinal correction surgery — RECRUITING
• Can External Vagus Nerve Stimulation Reduce Systemic Levels of Inflammatory Mediators in Duchenne Muscular Dystrophy Patients? — RECRUITING · NA
• An Open-label Long-term Follow-up Study of SAT-3247 for Participants With Duchenne Muscular Dystrophy Including Those Who Participated in SAT-3247-CL-101 — RECRUITING · PHASE2
• Invasive Home Ventilation in Denmark — RECRUITING
• Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders — RECRUITING
• Urinary Titin Biomarker in DMD — RECRUITING · NA
• DMD Gene Variants and Cardiac Dysfunction in Young Males With Dystrophinopathies — RECRUITING
• Long Term Follow-up for RGX-202 — RECRUITING
• Open-Label Extension Study of WVE-N531 in Patients With Duchenne Muscular Dystrophy — RECRUITING · PHASE2
• NS-089/NCNP-02-201 in Boys With Duchenne Muscular Dystrophy (DMD) — RECRUITING · PHASE2
• Trial of Cell Based Therapy for DMD — RECRUITING · PHASE1
• Duchenne Muscular Dystrophy and the Viscoelastic Properties of Upper Limb Muscles — RECRUITING
• Investigation of the Relationship Between Executive Functions and Occupational Performance of Children With Duchenne Muscular Dystrophy — RECRUITING
• Natural History of Duchenne Muscular Dystrophy — RECRUITING
• A Long-term Follow-up Study of Participants Who Received Delandistrogene Moxeparvovec (SRP-9001) in a Previous Clinical Study — RECRUITING · PHASE3
• Gamified Occupational Therapy for Adolescents With Duchenne Muscular Dystrophy — RECRUITING · NA
• The Effect of Dual-tasking Program on Cognitive and Physical Functions and Independence in Activities of Daily Living in Children With Duchenne Muscular Dystrophy: A Single-blind Randomized Controlled Trial — RECRUITING · NA
• Givinostat in Duchenne's Muscular Dystrophy Long-term Safety and Tolerability Study — RECRUITING · PHASE2
• Active NBS Study: Decentralised Monitoring Motor Development in Children With Duchenne Muscular Dystrophy or Spinal Muscular Atrophy Identified by Newborn Screening — RECRUITING · NA
• Open-label Study of WVE-N531 in Patients With Duchenne Muscular Dystrophy (FORWARD-53) — RECRUITING · PHASE1
• A PHASE 2A, RANDOMIZED, DOUBLE-BLIND, PLACEBO-CONTROLLED DOSE COMPARISON AND EXPLORATORY EFFICACY STUDY OF ORALLY ADMINISTERED SAT-3247 IN AMBULATORY DMD PATIENTS — RECRUITING · PHASE2
• Extracellular RNA Biomarkers of Duchenne Muscular Dystrophy — RECRUITING

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