Friedreich Ataxia Clinical Trials

79 clinical trials for Friedreich Ataxia across international registries, including 18 currently recruiting participants. Compare status, phase, eligibility criteria and locations.

• Study of LX2006 Gene Therapy in Friedreich Ataxia Cardiomyopathy — RECRUITING · PHASE2
• A Study to Learn How BIIB141 (Omaveloxolone) Affects the Health of Participants With Friedrich's Ataxia Who Took it During Pregnancy and/or During Breastfeeding and About the Health of Their Babies — RECRUITING
• A Study to Learn More About the Effects and Long-Term Safety of Omaveloxolone (BIIB141) in Children and Teens With Friedreich's Ataxia — RECRUITING · PHASE3
• Clinical Course Of Disease In Participants With FA-CM — RECRUITING
• An Open-Label Study of CTI-1601 in Subjects With Friedreich's Ataxia — RECRUITING · PHASE2
• Efficacy of Omaveloxolone Treatment for Dysphagia in French Patients With Friedreich's Ataxia — RECRUITING
• A Study to Learn More About the Long-Term Safety of BIIB141 (Omaveloxolone) in Participants With Friedreich's Ataxia Who Are Prescribed it by Their Own Doctors — RECRUITING
• Friedreich Ataxia Nerve Ultrasund — RECRUITING
• Patient-reported, Health Economic and Psychosocial Outcomes in Friedreich Ataxia — RECRUITING
• Phase IA and IB Study of AAVrh.10hFXN Gene Therapy for the Cardiomyopathy of Friedreich's Ataxia — RECRUITING · PHASE1
• Development and Validation of the FBIndex to Determine the Risk of Falls for Patients With Neuromuscular Disorders — RECRUITING
• The Use of Assistive Gait Devices Can Reduce the Risk of Falls in Patients With Neuromuscular Diseases Following a Training Period. — RECRUITING · NA
• Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study — RECRUITING
• Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford — RECRUITING
• A Multiple Ascending Dose Study of DT-216P2 in Patients With Friedreich's Ataxia — RECRUITING · PHASE1
• Efficacy of Stabilometric Platform to Improve Standing Balance in Patients With Friedreich's Ataxia — RECRUITING · NA
• Multiorgan complexity in Friedreich Ataxia — RECRUITING
• LONG-TERM OPEN-LABEL STUDY TO ASSESS THE SAFETY AND EFFICACY OF VATIQUINONE IN PATIENTS WITH FRIEDREICH ATAXIA — RECRUITING
• Longitudinal Analysis of Oral Communication in Friedreich's Ataxia — COMPLETED
• Digital Outcome Assessment Using AI Active Gaming and Motion Capture in Friedreich Ataxia — NOT_YET_RECRUITING
• Characterisation of the Cognitive Profile of Patients Suffering From Friedreich's Ataxia — ACTIVE_NOT_RECRUITING
• A Study to Assess Nomlabofusp in Adolescents and Children With Friedreich's Ataxia — TERMINATED · PHASE1
• Characterization of the Interruptions of the GAA Expansion and Study of Their Influence on the Severity of Friedreich's Ataxia — COMPLETED
• Evaluation of the Effect of Artesunate in Friedreich Ataxia (FA) — COMPLETED · PHASE1
• A Study to Find Out How BIIB141 (Omaveloxolone) is Processed in the Body and to Learn More About Its Safety in Participants With Friedreich's Ataxia Aged 2 to 15 Years Old — ACTIVE_NOT_RECRUITING · PHASE1
• A Study to Assess the Efficacy and Safety of Vatiquinone for the Treatment of Participants With Friedreich Ataxia — COMPLETED · PHASE2
• Long-Term Open-Label Study to Assess the Safety and Efficacy of Vatiquinone in Patients With Friedreich Ataxia — TERMINATED · PHASE3
• A PHASE 3 RANDOMIZED, DOUBLE-BLIND, PLACEBO-CONTROLLED, MULTICENTER STUDY TO EVALUATE THE EFFICACY AND SAFETY OF SUBCUTANEOUS NOMLABOFUSP IN SUBJECTS WITH FRIEDREICH'S ATAXIA — NOT_YET_RECRUITING · PHASE3
• A Study to Learn About the Effects and Safety of RTA 408 (Omaveloxolone) in People Aged 16 to 40 With Friedreich's Ataxia — COMPLETED · PHASE2
• Measurement of Frataxin mRNA in Biofluids — COMPLETED
• Gene Therapy for Cardiomyopathy Associated With Friedreich's Ataxia — ACTIVE_NOT_RECRUITING · PHASE1
• JIVE: AN OPEN-LABEL EXTENSION STUDY TO ASSESS THE LONG-TERM SAFETY, EFFICACY, PHARMACODYNAMICS, PHARMACOKINETICS, AND TOLERABILITY OF SUBCUTANEOUS CTI-1601 IN SUBJECTS WITH FRIEDREICH’S ATAXIA — NOT_YET_RECRUITING
• FRDA Investigator Initiated Study (IIS) With Elamipretide — COMPLETED · PHASE1
• A Study of ASP2016 in Adults Who Have Heart Disease Associated With Friedreich Ataxia — WITHDRAWN · PHASE1
• Respiratory Training in Friedreich's Ataxia — COMPLETED · NA
• A Study to Assess the Safety and Efficacy of Vatiquinone in Participants With Friedreich Ataxia — ACTIVE_NOT_RECRUITING · PHASE3
• A Study of Vatiquinone for the Treatment of Participants With Friedreich Ataxia — COMPLETED · PHASE2
• Understanding the Natural History Early in the Course or Presentation of Friedreich Ataxia — WITHDRAWN
• A Single Ascending Dose Study of DT-216P2 in Normal Healthy Participants — NOT_YET_RECRUITING · PHASE1
• Home Based Tele-exercise for People With Chronic Neurological Impairments — ACTIVE_NOT_RECRUITING · NA
• Neurology Measures in FA Children — COMPLETED
• Safety and Efficacy of Etravirine in Friedreich Ataxia Patients — COMPLETED · PHASE2
• A Double-Blind, Placebo-Controlled, Dose Exploration Study of CTI-1601 in Adult Subjects With Friedreich's Ataxia — COMPLETED · PHASE2
• A Natural History Study to TRACK Brain and Spinal Cord Changes in Individuals with Friedreich Ataxia (TRACK-FA) — ACTIVE_NOT_RECRUITING
• FA Clinical Outcome Measures — ACTIVE_NOT_RECRUITING
• Instrumented Data Exchange for Ataxia Study — COMPLETED
• Micronised Resveratrol as a Treatment for Friedreich Ataxia — COMPLETED · PHASE2
• Study to Evaluate Multiple Ascending Dose and Multi-Dose of DT-216 in Adult Patients With Friedreich Ataxia — COMPLETED · PHASE1
• Study of the Efficacy and Safety of Nicotinamide in Patients With Friedreich Ataxia — WITHDRAWN · PHASE2
• Evaluation of the Effects of Calcitriol's in the Neurological Symptoms of Friedreich's Ataxia Patients — COMPLETED · PHASE4

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