Infantile spinal muscular atrophy, type I [Werdnig-Hoffman] Clinical Trials

10 clinical trials for Infantile spinal muscular atrophy, type I [Werdnig-Hoffman] across international registries, including 5 currently recruiting participants. Compare status, phase, eligibility criteria and locations.

• Bone development in patients with spinal muscular atrophy (SMA) — RECRUITING
• Longitudinal Data Collection from Patients with Spinal Muscular Atrophy: The SMArtCARE Database — RECRUITING
• NMD-Leonardo - Mechanographical motion and performance analysis in patients with neuromuscular diseases and creation of a reference data record in a healthy cohort — RECRUITING
• Collection of cerebrospinal fluid and performing skin biopsies for obtaining fibroblasts for studies at the DZNE — RECRUITING
• Efficacy of exercises to Muscle MRI in patients with neuromuscular diseases and proband — RECRUITING
• Objectification of swallowing-related measurements in infants and young children with Spinal Muscular Atrophy — OTHER
• Dysphagia in Children with Spinal Muscular Atrophy — OTHER
• Development and evaluation of an IT-based Case Management to improve the care of patients with spinal muscular atrophy — OTHER
• Expanded Access Program to provide Nusinersen to Patients with infantile-onset spinal muscular atrophy (SMA) — OTHER
• Allogeneic Adipose Derived Stem Cells for Werdnig Hoffman Patients — OTHER · PHASE1

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