Limb Girdle Muscular Dystrophy Clinical Trials

33 clinical trials for Limb Girdle Muscular Dystrophy across international registries, including 4 currently recruiting participants. Compare status, phase, eligibility criteria and locations.

• Telecare Psychosocial and Cognitive Intervention for Children and Adolescents With Limb-Girdle Muscular Dystrophy — RECRUITING · NA
• A Study to Evaluate the Safety of AB-1003 (Previously LION-101) in Subjects With Genetic Confirmation of LGMD2I/R9 (Part1) — RECRUITING · PHASE1
• Molecular Analysis of Patients With Neuromuscular Disease — RECRUITING
• Congenital Muscle Disease Study of Patient and Family Reported Medical Information — RECRUITING
• 3 Year Follow up on ANO5 Patients — ACTIVE_NOT_RECRUITING
• MRI-phenotyping of Patients With Pathogenic Anoctamin 5 Variants — ACTIVE_NOT_RECRUITING
• LGMD R1 Natural History Study — ACTIVE_NOT_RECRUITING
• A Trial to Learn More About an Experimental Gene Therapy Called Bidridistrogene Xeboparvovec (SRP-9003) as a Possible Treatment for Limb Girdle Muscular Dystrophy 2E/R4 — ACTIVE_NOT_RECRUITING · PHASE3
• Defining Clinical Endpoints in Limb Girdle Muscular Dystrophy (LGMD) — COMPLETED
• A Gene Transfer Single Dose Study to Evaluate the Safety, Tolerability and Efficacy of SRP-9003 in Non-Ambulatory and Ambulatory Participants With Limb Girdle Muscular Dystrophy, Type 2E/R4 (Beta-Sarcoglycan [β-SG] Deficiency) — ACTIVE_NOT_RECRUITING · PHASE1
• Evolution of the Functional and Muscular State of Patients With Muscular Dystrophy 2A Belts — ACTIVE_NOT_RECRUITING
• A Study of the Natural History of Participants With LGMD2E/R4, LGMD2D/R3, LGMD2C/R5, and LGMD2A/R1 ≥ 4 Years of Age, Who Are Managed in Routine Clinical Practice — ACTIVE_NOT_RECRUITING
• A Gene Transfer Study to Evaluate the Safety, Tolerability and Efficacy of SRP-6004 in Ambulatory Participants With Limb Girdle Muscular Dystrophy, Type 2B/R2 (LGMD2B/R2, Dysferlin [DYSF] Related) — TERMINATED · PHASE1
• Study to Evaluate the Safety, Tolerability, and Efficacy of SRP-9004 Administered by Systemic Infusion in Limb Girdle Muscular Dystrophy Type 2D/R3 Participants in the United States — TERMINATED · PHASE1
• The Role of Muscle Ultrasound in Assessment of Sample of Patients With Limb-girdle Muscular Dystrophy — OTHER
• Rehabilitation in Muscular Dystrophies From the Hospital Facility to the Home: Pilot Project [RIMUDI] — OTHER · NA
• Global FKRP Registry — OTHER
• Study to Evaluate the Long-Term Safety, Tolerability, and Biological Activity of ATYR1940 in Participants With Limb Girdle and Facioscapulohumeral Muscular Dystrophy (FSHD) — COMPLETED · PHASE1
• Weekly Steroids in Muscular Dystrophy — COMPLETED · PHASE2
• Biomarker Development in LGMD2i — COMPLETED
• Schulze Muscular Dystrophy Ability Clinical Study — OTHER · NA
• Limb-Girdle Muscular Dystrophy Type 2I in Norway — OTHER
• A Study of Deflazacort (Emflaza®) in Participants With Limb-Girdle Muscular Dystrophy 2I (LGMD2I) — TERMINATED · PHASE3
• Stem Cell Therapy in Limb Girdle Muscular Dystrophy — WITHDRAWN · PHASE1
• Cell Therapy in Limb Girdle Muscular Dystrophy — WITHDRAWN · PHASE1
• Clinical Trial of Coenzyme Q10 and Lisinopril in Muscular Dystrophies — COMPLETED · PHASE2
• Genetic Characterization of Individuals With Limb Girdle Muscular Dystrophy — COMPLETED
• MRI on Persons With Mutations in POMT2 Gene (LGMD2N) — COMPLETED
• MRI and Muscle Involvement in Patients With Mutations in GMPPB — COMPLETED
• Safety Study of Transvenous Limb Perfusion in Human Muscular Dystrophy — COMPLETED · PHASE1
• Cardiac Outcome Measures in Children With Muscular Dystrophy — COMPLETED
• Cardiac Magnetic Resonance in Children With Muscular Dystrophy — COMPLETED
• Study Evaluating MYO-029 in Adult Muscular Dystrophy — COMPLETED · PHASE1

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