Mucopolysaccharidosis II Clinical Trials
37 clinical trials for Mucopolysaccharidosis II across international registries, including 7 currently recruiting participants. Compare status, phase, eligibility criteria and locations.
- ScreenPlus: A Comprehensive, Flexible, Multi-disorder Newborn Screening Program — RECRUITING
- An Extension Study of the Long-Term Safety, Tolerability, and Efficacy of Tividenofusp Alfa (DNL310) in Participants With Mucopolysaccharidosis Type II (MPS II) From Study DNLI-E-0002 or Study DNLI-E-0007 — RECRUITING · PHASE2
- Registry of Patients Diagnosed With Lysosomal Storage Diseases — RECRUITING
- MPS (RaDiCo Cohort) (RaDiCo-MPS) — RECRUITING
- An Extension Study of JR-141 to Evaluate the Long-term Safety and Efficacy in MPS II (Hunter Syndrome) Subjects — RECRUITING · PHASE3
- UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells — RECRUITING · PHASE1
- A Study to Determine the Efficacy and Safety of Tividenofusp Alfa (DNL310) vs Idursulfase in Pediatric and Young Adult Participants With Neuronopathic (nMPS II) or Non-Neuronopathic Mucopolysaccharidosis Type II (nnMPS II) — RECRUITING · PHASE2
- Long Term Follow-up (LTFU) of Subjects Who Received SB-318, SB-913, or SB-FIX — TERMINATED
- A Phase III Study of JR-141 in Patients With Mucopolysaccharidosis II (STARLIGHT) — ACTIVE_NOT_RECRUITING · PHASE3
- Gene Therapy With Modified Autologous Hematopoietic Stem Cells for Patients With Mucopolysaccharidosis Type II — ACTIVE_NOT_RECRUITING · PHASE1
- Study to Evaluate the Safety and Efficacy of Adalimumab in MPS I, II, and VI — ACTIVE_NOT_RECRUITING · PHASE1
- Baby Detect : Genomic Newborn Screening — COMPLETED
- A Study of Tividenofusp Alfa (DNL310) in Pediatric Participants With Hunter Syndrome — ACTIVE_NOT_RECRUITING · PHASE1
- An Extension Study of JR-141-BR21 in Patients With Mucopolysaccharidosis II — ACTIVE_NOT_RECRUITING · PHASE2
- A Study of JR-141 in Patients With Mucopolysaccharidosis II (BR21) — COMPLETED · PHASE2
- An Extension Study of JR-141 in Patients With Mucopolysaccharidosis Type II — ACTIVE_NOT_RECRUITING · PHASE2
- A Study to Evaluate the Safety, Tolerability, PK and PD of Intracerebroventricular GC1123 in Patients with MPS Ⅱ — ACTIVE_NOT_RECRUITING · PHASE1
- MPS II Immunophenotyping — TERMINATED
- A Study of Potential Treatment-Responsive Biomarkers and Clinical Outcomes in Hunter Syndrome — COMPLETED
- Safety and Efficacy of HMI-203 in ERT-Treated Adults With MPS II — WITHDRAWN · PHASE1
- Biomarkers for Hunter Syndrome — TERMINATED
- A Study of JR-141 in Patients With Mucopolysaccharidosis II — COMPLETED · PHASE2
- A Study of JR-141 in Patients With Mucopolysaccharidosis Type II — COMPLETED · PHASE1
- Ascending Dose Study of Genome Editing by the Zinc Finger Nuclease (ZFN) Therapeutic SB-913 in Subjects With MPS II — TERMINATED · PHASE1
- Mucopolysaccharidosis Type II Observational — WITHDRAWN
- Mucopolysaccharidosis Type II Natural History — COMPLETED
- Long-term Follow-Up for RGX-121 — OTHER
- Extension of Study TKT024 Evaluating Long-Term Safety and Clinical Outcomes in MPS II Patients Receiving Idursulfase — COMPLETED · PHASE2
- Iduronate-2-sulfatase Enzyme Replacement Therapy in Mucopolysaccharidosis II (MPS II) — COMPLETED · PHASE2
- Safety and Clinical Outcomes in Hunter Syndrome Patients 5 Years of Age and Younger Receiving Idursulfase Therapy — COMPLETED · PHASE4
- Safety and Dose Ranging Study of Insulin Receptor MoAb-IDS Fusion Protein in Patients With Hunter Syndrome — COMPLETED · PHASE1
- Clinical Trial of Growth Hormone in MPS I, II, and VI — TERMINATED · PHASE2
- A Study to Test the Possibility of Cross Reaction Induced by the Idursulfase Drug to GSK2788723 — COMPLETED
- Study of Idursulfase-beta (GC1111) in Hunter Syndrome — OTHER · PHASE2
- Study to Detect Unrecognized Mucopolysaccharidosis in Children Visiting Rheumatology, Hand or Skeletal Dysplasia Clinics — TERMINATED
- To Evaluate the Safety and Efficacy of GC1111 (Recombinant Human Iduronate-2-sulfatase) in Hunter Syndrome Patients — COMPLETED · PHASE1
- Phase I/II Study of Retroviral-Mediated Transfer of Iduronate-2-Sulfatase Gene Into Lymphocytes of Patients With Mucopolysaccharidosis II (Mild Hunter Syndrome) — COMPLETED · PHASE1
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