Mucopolysaccharidosis VII Clinical Trials

8 clinical trials for Mucopolysaccharidosis VII across international registries, including 4 currently recruiting participants. Compare status, phase, eligibility criteria and locations.

• ScreenPlus: A Comprehensive, Flexible, Multi-disorder Newborn Screening Program — RECRUITING
• Mucopolysaccharidosis VII Disease Monitoring Program — RECRUITING
• Registry of Patients Diagnosed With Lysosomal Storage Diseases — RECRUITING
• MPS (RaDiCo Cohort) (RaDiCo-MPS) — RECRUITING
• Expanded Access to Mepsevii — OTHER
• Baby Detect : Genomic Newborn Screening — COMPLETED
• A Study of UX003 Recombinant Human Beta-Glucuronidase (rhGUS) Enzyme Replacement Therapy in Subjects With Mucopolysaccharidosis Type 7, Sly Syndrome (MPS 7) — COMPLETED · PHASE3
• Study of UX003 Recombinant Human Beta-Glucuronidase (rhGUS) Enzyme Replacement Treatment in Mucopolysaccharidosis Type 7, Sly Syndrome (MPS 7) Patients Less Than 5 Years of Age — COMPLETED · PHASE2

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