Muscular Dystrophy, Duchenne Clinical Trials

48 clinical trials for Muscular Dystrophy, Duchenne across international registries, including 4 currently recruiting participants. Compare status, phase, eligibility criteria and locations.

• Efficacy, Safety, and Tolerability of Zeleciment Rostudirsen (DYNE-251) Administered Intravenously Every 4 Weeks in Ambulatory Participants With Duchenne Muscular Dystrophy (FORZETTO) — RECRUITING · PHASE3
• Development of Non-Invasive Prenatal Diagnosis for Single Gene Disorders — RECRUITING
• The Effect of a Muscle-mimicking, Fabric-type Shoulder Orthosis on Functional Movements of the Upper Limb in Patients With Neuromuscular Disorder — RECRUITING · NA
• Transcriptomic Analysis to Put an End to Misdiagnosis in Patients With Rare Muscle Diseases — RECRUITING · NA
• Managed Access Program for Del-zota in Participants With DMD Mutations Amenable to Exon 44 Skipping — OTHER
• Study of Genotype and Phenotype Characterization in Duchenne Muscular Dystrophy With Small Mutations — COMPLETED
• A Study of Deramiocel (CAP-1002) in Ambulatory and Non-Ambulatory Patients With Duchenne Muscular Dystrophy — ACTIVE_NOT_RECRUITING · PHASE3
• A Multicenter Cohort Study of Duchenne and Becker Muscular Dystrophy in Western Chinese Children — NOT_YET_RECRUITING
• Long-Term Outcomes of Ataluren in Duchenne Muscular Dystrophy — COMPLETED · PHASE3
• A Study to Compare Safety and Efficacy of High Doses of Eteplirsen in Participants With Duchenne Muscular Dystrophy (DMD) (MIS51ON) — ACTIVE_NOT_RECRUITING · PHASE3
• Registry of Translarna (Ataluren) in Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD) — COMPLETED
• Study of Fordadistrogene Movaparvovec in Early Stage Duchenne Muscular Dystrophy — TERMINATED · PHASE2
• A Study of CAP-1002 in Ambulatory and Non-Ambulatory Patients With Duchenne Muscular Dystrophy — COMPLETED · PHASE2
• Regular Physical Exercise in Duchenne Muscular Dystrophy — COMPLETED
• A Randomized, Double-blind, Placebo-controlled Study of Delandistrogene Moxeparvovec (SRP-9001) for Duchenne Muscular Dystrophy (DMD) — COMPLETED · PHASE1
• An Open-Label Extension Study for Patients With Duchenne Muscular Dystrophy Who Participated in Studies of SRP-5051 (Vesleteplirsen) — TERMINATED · PHASE1
• Characterization of DupEx2 Duchenne Muscular Dystrophy — OTHER
• Spironolactone Versus Prednisolone in DMD — TERMINATED · PHASE1
• Phase 1/2 Study in Boys With Duchenne Muscular Dystrophy — COMPLETED · PHASE1
• Effects of Parental Influence on Physical Activity Level and Participation in Children With Duchenne Muscular Dystrophy — COMPLETED
• A Study to Evaluate the Safety, Tolerability, and Pharmacokinetics of a Single Dose of SRP-5051 (Vesleteplirsen) in Patients With Duchenne Muscular Dystrophy (DMD) — COMPLETED · PHASE1
• Phase III Study of Edasalonexent in Boys With Duchenne Muscular Dystrophy — COMPLETED · PHASE3
• Validating Cardiac MRI Biomarkers and Genotype-Phenotype Correlations for DMD — COMPLETED · NA
• The Efficacy and Safety of Metoprolol as add-on Treatment to Standard of Care in Preventing Cardiomyopathy in Patients With DMD — OTHER · PHASE3
• Double Push Acoustic Radiation Force (DP ARF) Ultrasound for Monitoring Degeneration in Duchenne Muscular Dystrophy — COMPLETED
• Safety Study of BLS-M22 in Healthy Volunteers — COMPLETED · PHASE1
• A Study to Assess the Efficacy and Safety of MNK-1411 in Duchenne Muscular Dystrophy — TERMINATED · PHASE2
• The Effects of Trunk Exercises on Upper Extremity and Respiratory Functions in DMD — COMPLETED · NA
• The Expanded Access Use of Viltolarsen in Duchenne Muscular Dystrophy With Confirmed Exon 53 Amenable Mutation — OTHER
• An Extension Study of Ataluren (PTC124) in Participants With Nonsense Mutation Dystrophinopathy — TERMINATED · PHASE3
• Phase 3 Study of Ataluren in Participants With Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD) — COMPLETED · PHASE3
• Safety Study of Eteplirsen to Treat Advanced Stage Duchenne Muscular Dystrophy — COMPLETED · PHASE2
• User-centred Assistive System for Arm Functions in Neuromuscular Subjects — COMPLETED · NA
• Non-invasive Imaging of Muscle Structure in Duchenne Muscular Dystrophy Using Multispectral Optoacoustic Tomography — COMPLETED · NA
• A Study of Tadalafil for Duchenne Muscular Dystrophy — TERMINATED · PHASE3
• Rimeporide in Patients With Duchenne Muscular Dystrophy — COMPLETED · PHASE1
• Assessment of Cardiopulmonary Function in Duchenne Muscular Dystrophy — COMPLETED
• Effect of EPA and DHA in the Inflammation and Metabolic Disorders in DMD/DMB Patients — COMPLETED · NA
• Phase III Study of Idebenone in Duchenne Muscular Dystrophy (DMD) — COMPLETED · PHASE3
• Phase II Study of NPC-14 (Arbekacin Sulfate) to Explore Safety, Tolerability, and Efficacy in Duchenne Muscular Dystrophy — OTHER · PHASE2
• Modified Diet Trial: A Study of SMT C1100 in Paediatric Patients With DMD Who Follow a Balanced Diet — COMPLETED · PHASE1
• KUL0401: An Open-label Pilot Study of Oxatomide in Steroid-Naive Duchenne Muscular Dystrophy — COMPLETED · PHASE2
• Creatine and Glutamine in Steroid-Naive Duchenne Muscular Dystrophy — COMPLETED · PHASE2
• Study of Daily Pentoxifylline as a Rescue Treatment in Duchenne Muscular Dystrophy — COMPLETED · PHASE1
• Pentoxifylline in Duchenne Muscular Dystrophy — COMPLETED · PHASE1
• An Open-label Pilot Study of Coenzyme Q10 in Steroid-Treated Duchenne Muscular Dystrophy — COMPLETED · PHASE2
• Effect of Oral Glutamine on Muscle Mass and Function in Duchenne Muscular Dystrophy — COMPLETED · PHASE2
• A Multicenter Randomized Placebo-Controlled Double-Blind Study to Assess Efficacy and Safety of Glutamine and Creatine Monohydrate in Duchenne Muscular Dystrophy (DMD) — COMPLETED · PHASE3

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