Thalassemia Clinical Trials

161 clinical trials for Thalassemia across international registries, including 26 currently recruiting participants. Compare status, phase, eligibility criteria and locations.

• A Research Study Looking at Long-term Treatment With Etavopivat in People With Sickle Cell Disease or Thalassaemia — RECRUITING · PHASE3
• A Study to Provide Access to Mitapivat for Participants Who Previously Participated in an Agios-Sponsored Mitapivat Study — RECRUITING · PHASE4
• A Long-term Follow-up Study in Participants Who Received CTX001 — RECRUITING · PHASE3
• Safety and Efficacy of Hemoglobin F Inducers in Patients With Beta Thalassemia — RECRUITING · NA
• Low-Dose Liposomal Amphotericin B for Invasive Fungal Infection Prophylaxis in Neutropenic Children — RECRUITING
• ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders — RECRUITING
• A Study of Immune Suppression Treatment for People With Sickle Cell Disease or β-Thalassemia Who Are Going to Receive an Allogeneic Hematopoietic Cell Transplantation (HCT) — RECRUITING · PHASE2
• A Real-World Study to Evaluate Luspatercept in Adults With Transfusion-Dependent Beta-Thalassemia in the Middle East — RECRUITING
• Evaluation of Efficacy and Safety of a Single Dose of CTX001 in Participants With Transfusion-Dependent β-Thalassemia and Severe Sickle Cell Disease — RECRUITING · PHASE3
• A Study of Safety and Efficiency of AND017 in Patients With β-thalassemia — RECRUITING · PHASE2
• Atrial Fibrillation in Beta-Thalassemia — RECRUITING
• Determination of Red Cell Survival in Sickle Cell Disease and Other Hemoglobinopathies Using Biotin Labeling — RECRUITING · PHASE1
• Safety and Efficacy Evaluation of β-globin Restored Autologous Hematopoietic Stem Cells in β-thalassemia Major Patients — RECRUITING · PHASE1
• the Safety and Efficacy Evaluation of HGI-001 Injection in Patients With Transfusion-Dependent β-Thalassemia — RECRUITING · PHASE1
• the Safety and Efficacy Evaluation of HGI-002 Injection in Patients With Transfusion-Dependent α-Thalassemia — RECRUITING · PHASE1
• Evaluating Safety and Efficacy of Lentiviral-transduced CD34+ HSCs in Β-thalassaemia Patients. — RECRUITING · PHASE1
• A Phase 1 Study of Gene-modified Autologous Hematopoietic Stem Cell (BD211) Treating β-thalassemia Major — RECRUITING · PHASE1
• Safety and Efficacy of Gene Modified Autologous Hematopoietic Stem Cells to Treat Transfusion-dependent Beta-thalassemia — RECRUITING · NA
• European Rare Blood Disorders Platform (ENROL) — RECRUITING
• RADeep Multicenter European Epidemiological Platform for Patients Diagnosed With Rare Anemia Disorders (RADs) — RECRUITING
• AN OPEN-LABEL, DOSE-ESCALATION, DOSE-FINDING, AND PROOF-OF-CONCEPT TRIAL OF SP-420 IN SUBJECTS WITH TRANSFUSION-DEPENDENT ALPHA- OR BETA-THALASSEMIA OR LOW-RISK MYELODYSPLASTIC SYNDROMES — RECRUITING
• NOVEL TRANSPLANT STRATEGY FOR HIGH-RISK THALASSEMIA PATIENTS A PHASE I/II TRAIL OF EARLY FLUDARABINE FOLLOWED BY ABATACEPT AND SIROLIMUS IMMUNOSUPPRESSION (THAL-FABS STUDY) — RECRUITING · PHASE1
• A PHASE 3, DOUBLE-BLIND, RANDOMIZED, PLACEBO-CONTROLLED, MULTICENTER STUDY EVALUATING THE EFFICACY AND SAFETY OFMITAPIVAT IN SUBJECTS WITH TRANSFUSION-DEPENDENT ALPHA OR BETA-THALASSEMIA (ENERGIZE-T) — RECRUITING · PHASE3
• A PHASE 3, DOUBLE-BLIND, RANDOMIZED, PLACEBO CONBTROLLED, MULTI-CENTRE STUDY EVALUATING THE EFFICACY AND SAFETY OF MITAPIVAT IN SUBJECTS WITH NON-TRANSFUSION-DEPENDENT ALPHA- OR BETA-THALASSEMIA (ENERGIZE) — RECRUITING · PHASE3
• A PHASE 2, OPEN-LABEL, MULTICENTER STUDY TO DETERMINE THE EFFICACY, SAFETY, PHARMACOKINETICS, AND PHARMACODYNAMICS OF AG-348 IN ADULT SUBJECTS WITH NON-TRANSFUSION-DEPENDENT THALASSEMIA — RECRUITING · PHASE2
• A PHASE 3, DOUBLE-BLIND, RANDOMIZED, PLACEBO-CONTROLLED, MULTICENTER STUDY TO DETERMINE THE EFFICACY AND SAFETY OF LUSPATERCEPT (ACE-536) VERSUS PLACEBO IN ADULTS WHO REQUIRE REGULAR RED BLOOD CELL TRANSFUSIONS DUE TO BETA ()-THALASSEMIA — RECRUITING · PHASE3
• A Study to Investigate the Safety, Tolerability, Efficacy, Pharmacokinetics, And Pharmacodynamics of Bitopertin (RO4917838) in Adults with Non Transfusion Dependent β-Thalassemia. — TERMINATED · PHASE2
• Effect of Exercise on Body Composition and Bone Health in Patients With Thalassemia — ACTIVE_NOT_RECRUITING · NA
• Dexamethasone, Intravenous Injection of Human Immunoglobulin, and Increased Infusion of Mononuclear Cells to Reduce Donor Specific Antibodies in Haploidentical Hematopoietic Stem Cell Transplantation — NOT_YET_RECRUITING · PHASE2
• CINC424A2X01B Rollover Protocol — ACTIVE_NOT_RECRUITING · PHASE4
• Evaluation of Safety and Efficacy of CTX001 in Pediatric Participants With Transfusion-Dependent β-Thalassemia (TDT) — ACTIVE_NOT_RECRUITING · PHASE3
• A Study of SNH-119014 in Adult Participants With Non-transfusion-dependent Thalassemia (NTDT) — NOT_YET_RECRUITING · PHASE2
• A Study to Determine the Efficacy, Safety, Pharmacokinetics, and Pharmacodynamics of AG-348 in Adult Participants With Non-transfusion-dependent Thalassemia — ACTIVE_NOT_RECRUITING · PHASE2
• Bone Marrow and Kidney Transplant for Patients With Chronic Kidney Disease and Blood Disorders — COMPLETED · NA
• A Blood Stem Cell Transplant for Sickle Cell Disease — ACTIVE_NOT_RECRUITING · PHASE1
• Multicenter Observational Study on Myocardial Iron Overload in 3 Multitransfused Populations — COMPLETED
• Evaluation of the Quality of Life in Patients With Chronic Iron Overload Due to Hemoglobinopathies in Greece. — NOT_YET_RECRUITING
• A Study on the Effect of Etavopivat on Heart Rhythm in Healthy Participants — COMPLETED · PHASE1
• A Research Study Looking at a Single Dose of Etavopivat in Healthy Chinese Participants — COMPLETED · PHASE1
• A Safety and Efficacy Study Evaluating CTX001 in Participants With Transfusion-Dependent β-Thalassemia — COMPLETED · PHASE2
• A Study of Etavopivat in Patients With Thalassemia or Sickle Cell Disease — COMPLETED · PHASE2
• Effect of L-Glutamine on Pulmonary Artery Pressure in Patients With Non-Transfusion-Dependent Thalassemia — COMPLETED · PHASE2
• Impact of Virtual Reality on Pain and Anxiety During Intravenous Cannulation Procedures Among Thalassemia Patients in UAE. — COMPLETED · NA
• Fludarabine Phosphate, Cyclophosphamide, Total Body Irradiation, and Donor Stem Cell Transplant in Treating Patients With Blood Cancer — TERMINATED · PHASE2
• A Study of IMR-687 in Subjects With Beta Thalassemia — TERMINATED · PHASE2
• Pregnancy and Childbirth in Women with Thalassemia Yesterday and Today — COMPLETED
• Safety and Efficacy of Immunomodulator Drug Thalidomide in Multi-transfused Thalassemia Patients — COMPLETED · NA
• Long-term Clinical Study of CN128 in Thalassemia With Sever Liver Iron Overloaded Patients — COMPLETED · PHASE2
• Nonmyeloablative Peripheral Blood Mobilized Hematopoietic Precursor Cell Transplantation for Sickle Cell Disease and Beta-thalassemia in People With Higher Risk of Transplant Failure — ACTIVE_NOT_RECRUITING · PHASE2
• Inhibitory Effect of a Polyphenol Supplement on Dietary Iron Absorption in Adults with Thalassemia — COMPLETED · NA

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