A PHASE 1/2, MULTICENTER, OPEN-LABEL, DOSE ESCALATION AND EXPANSION CLINICAL STUDY TO EVALUATE THE SAFETY, TOLERABILITY AND PRELIMINARY EFFICACY OF ASP2957 IN MALE PARTICIPANTS WITH INVASIVE VENTILATOR-DEPENDENT X-LINKED MYOTUBULAR MYOPATHY

Registry ID

2957-CL-0101

Source registry

HEALTH_CANADA

Status

Pending

Phase

PHASE1

Study type

INTERVENTIONAL

Sponsor

ASTELLAS PHARMA CANADA INC

Last update

2025-07-30

Conditions

• X-LINKED MYOTUBULAR MYOPATHY

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