A MULTICENTER, RANDOMIZED, OPERATIONALLY SEAMLESS PHASE 2/3 STUDY TO EVALUATE THE EFFICACY AND SAFETY OF BMN 333 VERSUS VOSORITIDE IN CHILDREN WITH ACHONDROPLASIA
- Registry ID
- 333-301
- Source registry
- HEALTH_CANADA
- Status
- Pending
- Phase
- PHASE2
- Study type
- INTERVENTIONAL
- Sponsor
- BIOMARIN PHARMACEUTICAL INC
- Last update
- 2026-01-22
Conditions
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