AN OPEN-LABEL EXTENSION STUDY TO EVALUATE THE LONG-TERM EFFECTS OF ACE-083 IN PATIENTS WITH FSHD PREVIOUSLY ENROLLED IN STUDY A083-02 AND IN PATIENTS WITH CMT DISEASE TYPES 1 AND X PREVIOUSLY ENROLLED IN STUDY A083-03
- Registry ID
- A083-04
- Source registry
- HEALTH_CANADA
- Status
- Ongoing
- Study type
- INTERVENTIONAL
- Sponsor
- ACCELERON PHARMA INC
- Start date
- 2019-07-24
- Last update
- 2019-02-18
Conditions
- FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY
- CHARCOT-MARIE-TOOTH DISEASE TYPE 1A
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