A ROLLOVER STUDY TO PROVIDE CONTINUED ACCESS TO MITAPIVAT FOR PARTICIPANTS WHO PREVIOUSLY COMPLETED AN AGIOS-SPONSORED MITAPIVAT STUDY
- Registry ID
- AG348-C-025
- Source registry
- HEALTH_CANADA
- Status
- Ongoing
- Study type
- INTERVENTIONAL
- Sponsor
- AGIOS PHARMACEUTICALS INC
- Start date
- 2024-03-29
- Last update
- 2023-08-17
Conditions
- PYRUVATE KINASE DEFICIENCY
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- A PHASE 3, MULTICENTER, RANDOMIZED, DOUBLE-BLIND, PLACEBO-CONTROLLED STUDY TO EVALUATE THE EFFICACY AND SAFETY OF MITAPIVAT IN PEDIATRIC SUBJECTS WITH PYRUVATE KINASE DEFICIENCY WHO ARE NOT REGULARLY TRANSFUSED, FOLLOWED BY A 5-YEAR OPEN-LABEL EXTENSION PERIOD
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