LONG-TERM EXTENSION (LTE) STUDY TO CHARACTERIZE THE SAFETY AND EFFICACY OF DANICOPAN AS AN ADD-ON THERAPY TO A COMPLEMENT COMPONENT 5 INHIBITOR (C5I) IN PATIENTS WITH PAROXYSMAL NOCTURNAL HEMOGLOBINURIA (PNH) PREVIOUSLY TREATED WITH DANICOPAN IN AN ALEXION-SPONSORED CLINICAL STUDY

Registry ID

ALXN2040-PNH-303

Source registry

HEALTH_CANADA

Status

Ongoing

Study type

INTERVENTIONAL

Sponsor

ALEXION PHARMACEUTICALS INC

Start date

2025-06-02

Last update

2022-11-21

Conditions

• PAROXYSMAL NOCTURNAL HEMOGLOBINURIA

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