MULTI-CENTER, DOSE-ESCALATION STUDY, TO ASSESS SAFETY, TOLERABILITY AND EFFICACY OF INTRAVENOUS CABALETTA® IN OPMD PATIENTS
- Registry ID
- BBCO-001
- Source registry
- HEALTH_CANADA
- Status
- Ongoing
- Study type
- INTERVENTIONAL
- Sponsor
- BIOBLAST PHARMA LTD
- Start date
- 2015-03-20
- Last update
- 2014-09-15
Conditions
- OCULOPHARYNGEAL MUSCULAR DYSTROPHY (OPMD)
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