AN OPEN-LABEL EXTENSION TO INVESTIGATE THE LONG-TERM SAFETY, TOLERABILITY, AND
EFFICACY OF DNL310 IN PATIENTS WITH MUCOPOLYSACCHARIDOSIS TYPE II (MPS II)
FROM STUDY DNLI-E-0002 OR STUDY DNLI-E-0007
- Registry ID
- DNLI-E-0008
- Source registry
- HEALTH_CANADA
- Status
- Ongoing
- Study type
- INTERVENTIONAL
- Sponsor
- DENALI THERAPEUTICS INC.
- Start date
- 2025-04-04
- Last update
- 2023-10-30
Conditions
- MUCOPOLYSACCHARIDOSIS TYPE II (MPS II)
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