"A PHASE 1/2 STUDY TO EVALUATE THE SAFETY AND EFFICACY OF A SINGLE DOSE OF AUTOLOGOUS CLUSTERED REGULARLY INTERSPACED SHORT PALINDROMIC REPEATS GENE-EDITED CD34+ HUMAN HEMATOPOIETIC STEM AND PROGENITOR CELLS (EDIT-301) IN SUBJECTS WITH SEVERE SICKLE CELL DISEASE"

Registry ID
EM-SCD-301-001
Source registry
HEALTH_CANADA
Status
Ongoing
Phase
PHASE1
Study type
INTERVENTIONAL
Sponsor
EDITAS MEDICINE, INC.
Start date
2022-03-18
Last update
2021-06-30

Conditions

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