Full title of the trial : A Single Centre, Open-Label, Bridging Study of the Safety, Pharmacokinetics and Efficacy of Recombinant Human Acid Alpha-Glucosidase (rhGAA) Treatment in Patients with Late-Onset Pompe Disease (Glycogen Storage Disease Type II)
- Registry ID
- EUCTR2005-002829-31
- Source registry
- EUCTR
- Status
- Completed
- Phase
- PHASE2
- Sponsor
- Genzyme Europe BV
- Start date
- 2005-08-19
- Completion date
- 2006-07-13
- Last update
- 2026-08-16
Conditions
- Glycogen Storage Disease type II (Pompe´s disease)
Summary
Study the Safety, Pharmacokinetics and Efficacy of Recombinant Human Acid Alpha-Glucosidase (rhGAA) Treatment in Patients with Late-Onset Pompe Disease (Glycogen Storage Disease Type II)
Locations
View on source registry