A clinical trial to study the effects of genetically modified patients' skin stem cells

Registry ID
EUCTR2011-003212-22
Source registry
EUCTR
Status
Completed
Phase
PHASE1
Sponsor
GOSH/ICH Joint Research & Development Office
Start date
2013-06-03
Completion date
2017-09-30
Last update
2026-08-16

Conditions

Summary

(1) Generation of SPINK5 gene modified keratinocytes (including keratinocyte stem cells)(self-renewing cells) from patients with Netherton Syndrome (2) Generation of epithelial sheets for auto-grafting (tissue transplant from one part of the body to another in same individual) using gene corrected keratinocyte stem cells (3) Grafting of gene corrected epithelial sheets onto patients with Netherton Syndrome (4) To examine long-term safety and efficacy of the treatment

Locations

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