Phase 2A clinical trial conducted on children affected by Rett syndrome and who are casually administered with the experimental treatment, EPI-743, compared versus the se of placebo.

Registry ID

EUCTR2012-005021-76

Source registry

EUCTR

Status

Completed

Phase

PHASE2

Sponsor

EDISON PHARMACEUTICALS INC.

Start date

2013-01-31

Last update

2026-08-16

Conditions

• Rett Syndrome

Summary

To evaluate the efficacy of EPI-743 in patients with Rett syndrome, on disease progression as assessed by the Rett Syndrome clinical Severity Score (RSSS)

Locations

• , , Italy

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