A study to evaluate the effect of ALN-PCSSC treatment in patients with Homozygous Familial Hypercholesterolemia

Registry ID

EUCTR2016-003376-49

Source registry

EUCTR

Status

Completed

Phase

PHASE2

Sponsor

The Medicines Company

Start date

2017-01-09

Completion date

2018-10-08

Last update

2026-08-16

Conditions

• Homozygous Familial Hypercholesterolemia

Summary

To characterize the effect of 90 and 180 days of subcutaneous ALN-PCSSC on the percentage change from Day 1 in low-density lipoprotein cholesterol (LDL-C) in subjects with homozygous familial hypercholesterolemia.

Locations

• , , Netherlands

Related clinical trials

• The Rogosin Institute Homozygous Familial Hypercholesterolemia Repository
• HoFH, the International Clinical Collaborators Registry
• NGGT006 Gene Therapy for Homozygous Familial Hypercholesterolemia

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