A LONG-TERM EXTENSION TRIAL INVESTIGATING THE SAFETY AND EFFICACY OF GTX-102 IN PATIENTS WITH ANGELMAN SYNDROME

Registry ID
GTX-102-CL302
Source registry
HEALTH_CANADA
Status
Ongoing
Study type
INTERVENTIONAL
Sponsor
ULTRAGENYX PHARMACEUTICAL INC
Start date
2024-09-26
Last update
2024-05-17

Conditions

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