A LONG-TERM EXTENSION TRIAL INVESTIGATING THE SAFETY AND EFFICACY OF GTX-102 IN PATIENTS WITH ANGELMAN SYNDROME
- Registry ID
- GTX-102-CL302
- Source registry
- HEALTH_CANADA
- Status
- Ongoing
- Study type
- INTERVENTIONAL
- Sponsor
- ULTRAGENYX PHARMACEUTICAL INC
- Start date
- 2024-09-26
- Last update
- 2024-05-17
Conditions
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