A PHASE 1/2A STUDY TO EVALUATE THE SAFETY, TOLERABILITY, PHARMACOKINETICS AND PHARMACODYNAMICS OF INTRATHECALLY ADMINISTERED ION717 IN PATIENTS WITH PRION DISEASE
- Registry ID
- ION717-CS2
- Source registry
- HEALTH_CANADA
- Status
- Ongoing
- Phase
- PHASE1
- Study type
- INTERVENTIONAL
- Sponsor
- IONIS PHARMACEUTICALS INC
- Start date
- 2024-01-23
- Last update
- 2023-05-11
Conditions
View on source registry