A PHASE 1/2A STUDY TO EVALUATE THE SAFETY, TOLERABILITY, PHARMACOKINETICS AND PHARMACODYNAMICS OF INTRATHECALLY ADMINISTERED ION717 IN PATIENTS WITH PRION DISEASE

Registry ID
ION717-CS2
Source registry
HEALTH_CANADA
Status
Ongoing
Phase
PHASE1
Study type
INTERVENTIONAL
Sponsor
IONIS PHARMACEUTICALS INC
Start date
2024-01-23
Last update
2023-05-11

Conditions

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