AN OPEN-LABEL DOSE-ESCALATION STUDY TO EVALUATE THE SAFETY, TOLERABILITY, PHARMACOKINETICS, AND PHARMACODYNAMICS OF MRNA-3745 IN PARTICIPANTS WITH GLYCOGEN STORAGE DISEASE TYPE 1A (GSD1A)
- Registry ID
- MRNA-3745-P102
- Source registry
- HEALTH_CANADA
- Status
- Ongoing
- Study type
- INTERVENTIONAL
- Sponsor
- MODERNATX, INC.
- Start date
- 2024-08-29
- Last update
- 2022-05-27
Conditions
- GLYCOGEN STORAGE DISEASE TYPE IA
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