AN OPEN-LABEL EXTENSION STUDY TO EVALUATE THE LONG-TERM SAFETY AND EFFICACY OF MARALIXIBAT IN THE TREATMENT OF SUBJECTS WITH PROGRESSIVE FAMILIAL INTRAHEPATIC CHOLESTASIS (PFIC)
- Registry ID
- MRX-503
- Source registry
- HEALTH_CANADA
- Status
- Closed
- Study type
- INTERVENTIONAL
- Sponsor
- MIRUM PHARMACEUTICALS, INC
- Completion date
- 2025-04-23
- Last update
- 2020-01-02
Conditions
- PROGRESSIVE FAMILIAL INTRAHEPATIC CHOLESTASIS
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