A RANDOMIZED TRIAL OF LOW VERSUS MODERATE EXPOSURE BUSULFAN FOR INFANTS WITH SEVERE COMBINED IMMUNODEFICIENCY (SCID) RECEIVING TCR¿¿+/CD19+ DEPLETED TRANSPLANTATION: A PHASE II STUDY BY THE PRIMARY IMMUNE DEFICIENCY TREATMENT CONSORTIUM (PIDTC) AND PEDIATRIC TRANSPLANTATION & CELLULAR THERAPY CONSORTIUM (PTCTC) PIDTC ¿CSIDE¿ PROTOCOL (CONDITIONING SCID INFANTS DIAGNOSED EARLY) PTCTC NMD1801
- Registry ID
- NMD1801
- Source registry
- HEALTH_CANADA
- Status
- Ongoing
- Phase
- PHASE2
- Study type
- INTERVENTIONAL
- Sponsor
- PEDIATRIC TRANSPLANTATION AND CELLULAR THERAPY CONSORTIUM
- Start date
- 2024-11-18
- Last update
- 2021-02-05
Conditions
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