EFFICACY AND SAFETY STUDY OF VATIQUINONE FOR THE TREATMENT OF MITOCHONDRIAL DISEASE SUBJECTS WITH REFRACTORY EPILEPSY (MIT-E)
- Registry ID
- PTC743-MIT-001-EP
- Source registry
- HEALTH_CANADA
- Status
- Closed
- Study type
- INTERVENTIONAL
- Sponsor
- PTC THERAPEUTICS INC
- Start date
- 2022-03-21
- Completion date
- 2022-08-17
- Last update
- 2021-12-10
Conditions
- MITOCHONDRIAL DISORDERS
- EPILEPSY
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