A DOUBLE-MASKED, RANDOMIZED, PLACEBO-CONTROLLED, PAIRED-EYE STUDY TO
EVALUATE THE EFFICACY, SAFETY AND TOLERABILITY OF SEPOFARSEN IN SUBJECTS WITH
LEBER CONGENITAL AMAUROSIS (LCA) DUE TO THE C.2991+1655A>G (P.CYS998X)
MUTATION IN THE CEP290 GENE
- Registry ID
- SB-110-007
- Source registry
- HEALTH_CANADA
- Status
- Ongoing
- Study type
- INTERVENTIONAL
- Sponsor
- LABORATOIRES THEA
- Start date
- 2025-08-11
- Last update
- 2024-12-19
Conditions
- LEBER CONGENITAL AMAUROSIS
View on source registry