CANCELLED - PHASE 1/2, OPEN-LABEL CLINICAL STUDY TO EVALUATE THE SAFETY AND EFFICACY OF INTRATHECAL TSHA101 GENE THERAPY FOR TREATMENT OF INFANTILE ONSET GM2 GANGLIOSIDOSIS

Registry ID
TSHA101-IST-001
Source registry
HEALTH_CANADA
Status
Pending
Phase
PHASE1
Study type
INTERVENTIONAL
Sponsor
QUEENS UNIVERSITY
Last update
2020-12-18

Conditions

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