CANCELLED - PHASE 1/2, OPEN-LABEL CLINICAL STUDY TO EVALUATE THE SAFETY AND EFFICACY OF INTRATHECAL TSHA101 GENE THERAPY FOR TREATMENT OF INFANTILE ONSET GM2 GANGLIOSIDOSIS
- Registry ID
- TSHA101-IST-001
- Source registry
- HEALTH_CANADA
- Status
- Pending
- Phase
- PHASE1
- Study type
- INTERVENTIONAL
- Sponsor
- QUEENS UNIVERSITY
- Last update
- 2020-12-18
Conditions
View on source registry