A PHASE 1B/2A OPEN-LABEL SINGLE ASCENDING DOSES (SAD) AND MULTIPLE ASCENDING DOSES (MAD) RESEARCH STUDY TO EVALUATE SAFETY, TOLERABILITY, PHARMACOKINETICS AND PHARMACODYNAMICS IN PARTICIPANTS WITH AATD PI*ZZ ON WVE-006 (RESTORAATION-2)

Registry ID

WVE-006-002

Source registry

HEALTH_CANADA

Status

Ongoing

Phase

PHASE1

Study type

INTERVENTIONAL

Sponsor

WAVE LIFE SCIENCES UK LTD

Start date

2024-08-06

Last update

2024-04-25

Conditions

• ALPHA-1 ANTITRYPSIN DEFICIENCY (AATD)

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