Facioscapulohumeral Muscular Dystrophy Clinical Trials

47 clinical trials for Facioscapulohumeral Muscular Dystrophy across international registries, including 13 currently recruiting participants. Compare status, phase, eligibility criteria and locations.

• Phase 2 Study Evaluating Apitegromab for the Treatment of FSHD — RECRUITING · PHASE2
• A Study to Evaluate Del-brax (Also Referred to as AOC 1020) in Participants With FSHD — RECRUITING · PHASE3
• Personalized Training for People With Rare Neuromuscular Disorders — RECRUITING · NA
• BetterLife FSHD: A Patient-driven Health and Research Platform — RECRUITING
• Biomarker Development for Muscular Dystrophies — RECRUITING
• Myotonic Dystrophy and Facioscapulohumeral Muscular Dystrophy Registry — RECRUITING
• A RANDOMIZED, DOUBLE-BLIND, PLACEBO-CONTROLLED, PHASE 3 STUDY TO EVALUATE THE EFFICACY AND SAFETY OF INTRAVENOUS AOC 1020 FOR THE TREATMENT OF FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY (FSHD) — RECRUITING · PHASE3
• A PHASE 2 OPEN-LABEL EXTENSION STUDY TO EVALUATE THE LONG-TERM SAFETY, TOLERABILITY, EFFICACY, AND PHARMACOKINETICS OF AOC 1020 ADMINISTERED INTRAVENOUSLY TO ADULT PARTICIPANTS WITH FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY (FSHD) — RECRUITING · PHASE2
• The United Kingdom Facioscapulohumeral Muscular Dystrophy Patient Registry — RECRUITING
• A BICENTRIC, RANDOMIZED, DOUBLE BLIND, PLACEBO-CONTROLLED PILOT STUDY TO EVALUATE THE EFFICACY AND SAFETY OF SATRALIZUMAB IN FSHD1 — RECRUITING
• A PHASE 1/2A DOSE-ESCALATING STUDY TO EVALUATE THE SAFETY, TOLERABILITY, PHARMACOKINETICS, AND PHARMACODYNAMICS OF ARO-DUX4 IN ADULT PATIENTS WITH FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY TYPE 1 — RECRUITING · PHASE1
• A PHASE 1/2A DOSE-ESCALATING STUDY TO EVALUATE THE SAFETY, TOLERABILITY, PHARMACOKINETICS, AND PHARMACODYNAMICS OF ARO-DUX4 IN ADULT PATIENTS AND ADOLESCENT PATIENTS WITH FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY TYPE 1 — RECRUITING · PHASE1
• AN OPEN-LABEL EXTENSION STUDY TO EVALUATE THE LONG-TERM EFFECTS OF ACE-083 IN PATIENTS WITH FSHD PREVIOUSLY ENROLLED IN STUDY A083-02 AND IN PATIENTS WITH CMT DISEASE TYPES 1 AND X PREVIOUSLY ENROLLED IN STUDY A083-03 — RECRUITING
• Magnetic Resonance Imaging and Spectroscopy Biomarkers for Facioscapulohumeral Muscular Dystrophy — ACTIVE_NOT_RECRUITING
• A First-in-human Study of EPI-321 in Facioscapulohumeral Muscular Dystrophy — ACTIVE_NOT_RECRUITING · PHASE1
• A Randomized, Double-blind, Placebo-controlled, Phase 3 Study to Evaluate the Efficacy and Safety of Intravenous AOC 1020 for the Treatment of Facioscapulohumeral Muscular Dystrophy (FSHD) — TERMINATED · PHASE3
• A Phase 1/2a Dose-Escalating Study to Evaluate the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of ARO-DUX4 in Adult Patients With Facioscapulohumeral Muscular Dystrophy Type 1 — TERMINATED · PHASE2
• A Study to Evaluate RO7204239 in Participants With Facioscapulohumeral Muscular Dystrophy — ACTIVE_NOT_RECRUITING · PHASE2
• Clinical Trial Readiness to Solve Barriers to Drug Development in FSHD — ACTIVE_NOT_RECRUITING
• A Phase II, Multicenter, Randomized, Placebo-Controlled, Double-Blind Study to Evaluate the Pharmacodynamics, Safety, Tolerability, Pharmacokinetics, and Efficacy of RO7204239 in Participants With Facioscapulohumeral Muscular Dystrophy — TERMINATED · PHASE2
• Quantitative Assessment of Orofacial Muscle Function in FSHD — COMPLETED · NA
• Ultrasound Detection of Early Facial Muscle Changes in FSHD: Thickness and Echo Intensity Findings — COMPLETED
• Efficacy and Safety of Losmapimod in Treating Participants With Facioscapulohumeral Muscular Dystrophy (FSHD) (REACH) — TERMINATED · PHASE3
• Efficacy and Safety of Losmapimod in Treating Subjects With Facioscapulohumeral Muscular Dystrophy (FSHD) With Open-Label Extension (OLE) — TERMINATED · PHASE2
• ADVANCED FSHD-COM: New Clinical Outcome Measures to Evaluate Non-ambulant FSHD Patients, a Pilot Study — ACTIVE_NOT_RECRUITING · NA
• A Phase 3 Global, Randomized, Double-Blind, Placebo-Controlled, 48-Week, Parallel-Group Study of the Efficacy and Safety of Losmapimod in Treating Patients With Facioscapulohumeral Muscular Dystrophy (FSHD) (REACH) — OTHER · PHASE3
• Efficacy and Safety of Losmapimod in Subjects With Facioscapulohumeral Muscular Dystrophy (FSHD) — COMPLETED · PHASE2
• At-Home Research Study for Patients With Autoimmune, Inflammatory, Genetic, Hematological, Infectious, Neurological, CNS, Oncological, Respiratory, Metabolic Conditions — COMPLETED
• Study to Evaluate the Long-Term Safety, Tolerability, and Biological Activity of ATYR1940 in Participants With Limb Girdle and Facioscapulohumeral Muscular Dystrophy (FSHD) — COMPLETED · PHASE1
• Evaluate Safety and Biological Activity of ATYR1940 in Participants With Early Onset Facioscapulohumeral Muscular Dystrophy — COMPLETED · PHASE1
• Evaluate Safety and Biological Activity of ATYR1940 in Participants With Limb Girdle Muscular Dystrophy 2B (LGMD2B) and Facioscapulohumeral Muscular Dystrophy (FSHD) — COMPLETED · PHASE1
• Unraveling Metabolic Involvement in Facioscapulohumeral Dystrophy Through Metabolomics — OTHER
• Effectiveness of Upper Extremity Rehabilitation in pwFSHD (Patient With Facioscapulohumeral Dystrophia) — COMPLETED
• Safety, Tolerability, Pharmacokinetics (PK), and Activity of ATYR1940 in Participants With Muscular Dystrophy - Study Extension — COMPLETED · PHASE1
• Study of Testosterone and rHGH in FSHD — COMPLETED · PHASE1
• A RANDOMIZED, DOUBLE-BLIND, PLACEBO-CONTROLLED, PHASE 1/2 STUDY TO EVALUATE THE SAFETY, TOLERABILITY, PHARMACOKINETICS, PHARMACODYNAMICS, AND EXPLORATORY EFFICACY OF AOC 1020 ADMINISTERED INTRAVENOUSLY TO ADULT PARTICIPANTS WITH FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY (FSHD) — COMPLETED · PHASE1
• Study of ACE-083 in Patients With Facioscapulohumeral Muscular Dystrophy (FSHD) — TERMINATED · PHASE2
• Extension Study to Evaluate the Long-Term Effects of ACE-083 in Patients With Facioscapulohumeral Muscular Dystrophy (FSHD) and Charcot-Marie Tooth (CMT) Disease Types 1 and X (CMT1 and CMTX) — TERMINATED · PHASE2
• Safety, Tolerability, Pharmacokinetics, and Biological Activity of ATYR1940 in Adult Participants With Muscular Dystrophy — COMPLETED · PHASE1
• Arm Cycling in Facioscapulohumeral Dystrophy (FSHD) Patients — COMPLETED · NA
• Effects Antioxidants Supplementation on Muscular Function Patients Facioscapulohumeral Dystrophy (FSHD) — COMPLETED · NA
• Bone Health in Facioscapulohumeral Muscular Dystrophy — COMPLETED
• Facioscapulohumeral Dystrophy in Children — COMPLETED
• Rasch-analysis of Clinical Severity in FSHD — COMPLETED
• A Multicenter Collaborative Study on the Clinical Features, Expression Profiling, and Quality of Life of Infantile Onset FSHD — COMPLETED
• Electrostimulation of Shoulder Girdle and Quadriceps Muscles in Facioscapulohumeral Muscular Dystrophy Patients — COMPLETED · NA
• Study Evaluating MYO-029 in Adult Muscular Dystrophy — COMPLETED · PHASE1

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