Rett Syndrome Clinical Trials

101 clinical trials for Rett Syndrome across international registries, including 18 currently recruiting participants. Compare status, phase, eligibility criteria and locations.

• Parent and Infant Inter(X)Action Intervention (PIXI) — RECRUITING · NA
• Rett Syndrome Registry — RECRUITING
• Cognitive Function in Rett Syndrome During Trofinetide Treatment — RECRUITING
• Lamivudine as a Novel Clinical Effort for Rett Syndrome — RECRUITING · PHASE2
• Safety and Preliminary Efficacy of TSHA-102 Gene Therapy in Pediatric Females Aged >2 to <4 Years With Rett Syndrome — RECRUITING · PHASE3
• Auditory EEG and Behavioral Assessments in Individuals With Rett Syndrome — RECRUITING
• Rett REVOLUTION Trial: An Exploratory Evaluation of the Safety and Efficacy of Vorinostat in Rett Syndrome — RECRUITING · PHASE1
• A Phase 3 randomized, double-blind, placebo-controlled, parallel group, multicenter study with open-label extension to evaluate the efficacy and safety of fenfluramine hydrochloride in study participants with Rett syndrome — RECRUITING · PHASE3
• To Investigate the Efficacy of Treatment With Oral NA-921 (Bionetide) Versus Placebo in Females With Rett Syndrome — RECRUITING · PHASE3
• The Rett Syndrome Global Registry — RECRUITING
• Validating Innovative Biosensors for Rett Autonomic Symptom Tracking — RECRUITING
• Neurophysiologic Biomarkers in Rett Syndrome — RECRUITING
• Gene Editing as a Therapeutic Approach for Rett Syndrome — RECRUITING
• Measuring Impact of Computer Gaming on Arm Use in Rett Syndrome — RECRUITING · NA
• REVEAL PEDIATRIC STUDY: AN OPEN-LABEL, RANDOMIZED, DOSE-ESCALATION AND DOSE-EXPANSION STUDY OF THE SAFETY TOLERABILITY AND EFFICACY OF A SINGLE IT ADMINISTRATION OF TSHA-102, AN AAV9-DELIVERED GT, FOR THE TREATMENT OF PEDIATRIC FEMALES WITH RTT — RECRUITING
• Diagnostics under sedation in people with intellectual disability or complex multiple disabilities in a medical center for adults with disabilities (MZEB) - secondary analysis of file data — RECRUITING
• GROWing Up With Rare GENEtic Syndromes — RECRUITING
• AN OPEN-LABEL, RANDOMIZED, DOSE-ESCALATION AND DOSE-EXPANSION STUDY OF THE SAFETY AND PRELIMINARY EFFICACY OF A SINGLE INTRATHECAL ADMINISTRATION OF TSHA-102, AN AAV9-DELIVERED GENE THERAPY, IN THE TREATMENT OF ADULT FEMALES WITH RETT SYNDROME — RECRUITING
• Phase 2A clinical trial conducted on children affected by Rett syndrome and who are casually administered with the experimental treatment, EPI-743, compared versus the se of placebo. — COMPLETED · PHASE2
• Repurposing mirtazapine in Rett syndrome: a multicentric open label Phase II study (MirtaRett Study). — TERMINATED · PHASE2
• Adapting a Psychosocial Support Intervention for the Rett Syndrome Community — NOT_YET_RECRUITING · NA
• A Pilot Study of an Antioxidant Cocktail vs. Placebo in the Treatment of Children and Adolescents With Rett Syndrome — NOT_YET_RECRUITING · PHASE2
• Web Intervention for Parents of Youth With Genetic Syndromes (WINGS) — ACTIVE_NOT_RECRUITING · NA
• A Phase 3 Study of Fenfluramine Hydrochloride in Rett Syndrome — NOT_YET_RECRUITING · PHASE3
• Double-blind, randomized, placebo-controlled study of Leriglitazone in pediatric Rett Syndrome — TERMINATED · PHASE2
• A Phase 1/2/3 Study of TSHA-102 Gene Therapy in Females With Rett Syndrome (REVEAL Pivotal Study) — ACTIVE_NOT_RECRUITING · PHASE3
• Early Check: Expanded Screening in Newborns — ACTIVE_NOT_RECRUITING
• A Novel, Regulated Gene Therapy (NGN-401) Study for Females With Rett Syndrome — ACTIVE_NOT_RECRUITING · PHASE3
• Single-Dose AAV-MECP2 Safety/Tolerability and Efficacy in Rett Syndrome — ACTIVE_NOT_RECRUITING · PHASE1
• Esketamine for the Treatment of Rett Syndrome — COMPLETED · PHASE1
• Technology-supported Motor Rehabilitation for People With Rett Syndrome — ACTIVE_NOT_RECRUITING · NA
• A PHASE 3 RANDOMIZED, DOUBLE-BLIND, PLACEBO-CONTROLLED, PARALLEL GROUP, MULTICENTER STUDY WITH OPEN-LABEL EXTENSION TO EVALUATE THE EFFICACY AND SAFETY OF FENFLURAMINE HYDROCHLORIDE IN STUDY PARTICIPANTS WITH RETT SYNDROME — NOT_YET_RECRUITING · PHASE3
• Efficacy and Safety of NTI164 in Children and Young Adults With Rett Syndrome — NOT_YET_RECRUITING · PHASE2
• Safety and Efficacy of TSHA-102 in Pediatric Females With Rett Syndrome (REVEAL Pediatric Study) — ACTIVE_NOT_RECRUITING · PHASE1
• Obi Medical Robot: Evaluating Effectiveness Related to Usability — ACTIVE_NOT_RECRUITING
• To Study the Efficacy & Safety of Oral NA-921 (Bionetide) in Girls and Women with Rett Syndrome — COMPLETED · PHASE2
• ASSESSING EMERALD AND MC10 BIOSTAMP nPOINT BIOSENSORS FOR RETT SYNDROME — COMPLETED
• Assessing the Safety and Efficacy of Full-Spectrum Medicinal Cannabis Plant Extract 0.08% THC (NTI164) in the Treatment of Rett Syndrome (RTT) — ACTIVE_NOT_RECRUITING · PHASE1
• Open-Label Extension Study of Trofinetide for Rett Syndrome — TERMINATED · PHASE3
• An Open-Label Study of Trofinetide for the Treatment of Girls Two to Five Years of Age Who Have Rett Syndrome — TERMINATED · PHASE2
• A Study to Evaluate Ketamine for the Treatment of Rett Syndrome — COMPLETED · PHASE2
• Open-Label Extension Study of Trofinetide for the Treatment of Girls and Women With Rett Syndrome — COMPLETED · PHASE3
• Study of Trofinetide for the Treatment of Girls and Women With Rett Syndrome (LAVENDER™) — COMPLETED · PHASE3
• Biomarkers in Rett Syndrome — OTHER
• The Diagnostic Experience of Male Rett Syndrome — OTHER
• Assessment of Nutritional and Growth Status in Rett Syndrome Patients — COMPLETED
• Intensive Anti-Scoliosis Postural Intervention for Individuals With Rett Syndrome Supported by a Smartphone Application — COMPLETED · NA
• ANAVEX2-73 Study in Pediatric Patients With Rett Syndrome — COMPLETED · PHASE2
• Protective Role of Pre-/ Post-biotics on Gut Inflammation, Dysbiosis, and Life Quality in Rett Syndrome (Biotics_RTT) — COMPLETED · NA
• Osteopathic Manipulative Treatment for Constipation in People With Rett Syndrome — COMPLETED · NA

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