X-linked Myotubular Myopathy Clinical Trials

12 clinical trials for X-linked Myotubular Myopathy across international registries, including 4 currently recruiting participants. Compare status, phase, eligibility criteria and locations.

• A Study to Check Liver Health in Boys With XLMTM, a Serious Genetic Muscle Condition — RECRUITING
• Study of ASP2957 in Male Participants With X-linked Myotubular Myopathy Who Need Ventilators — RECRUITING · PHASE1
• Myotubular and Centronuclear Myopathy Patient Registry — RECRUITING
• ASPIRO: A PHASE 1/2, RANDOMIZED, OPEN-LABEL, ASCENDING-DOSE, DELAYED-TREATMENT CONCURRENT CONTROL CLINICAL STUDY TO EVALUATE THE SAFETY AND PRELIMINARY EFFICACY OF AT132, AN AAV8-DELIVERED GENE THERAPY IN X-LINKED MYOTUBULAR MYOPATHY (XLMTM) PATIENTS — RECRUITING · PHASE1
• A Phase 1/2, Multicenter, Open-label, Dose Escalation and Expansion Clinical Study to Evaluate the Safety, Tolerability and Preliminary Efficacy of ASP2957 in Male Participants with Invasive Ventilator-dependent X-linked Myotubular Myopathy — NOT_YET_RECRUITING · PHASE2
• A Study of AT132 in Young Children With X-Linked Myotubular Myopathy (XLMTM) — ACTIVE_NOT_RECRUITING · PHASE2
• ASPIRO: A Phase 1/2/3, Randomized, Open-Label, Ascending-Dose, Delayed-Treatment Concurrent Control Clinical Study to Evaluate the Safety and Efficacy of AT132, an AAV8-Delivered Gene Therapy in X-Linked Myotubular Myopathy (XLMTM) Patients — TERMINATED · PHASE3
• A PHASE 1/2, MULTICENTER, OPEN-LABEL, DOSE ESCALATION AND EXPANSION CLINICAL STUDY TO EVALUATE THE SAFETY, TOLERABILITY AND PRELIMINARY EFFICACY OF ASP2957 IN MALE PARTICIPANTS WITH INVASIVE VENTILATOR-DEPENDENT X-LINKED MYOTUBULAR MYOPATHY — NOT_YET_RECRUITING · PHASE1
• Tamoxifen Therapy for Myotubular Myopathy — TERMINATED · PHASE1
• A Clinical Assessment Study in X-Linked Myotubular Myopathy (XLMTM) Subjects — COMPLETED
• Respiratory Muscle Function in Untreated X-Linked Myotubular Myopathy (XLMTM) — COMPLETED
• Myotubular Myopathy Event Study — COMPLETED

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