A PHASE 1/2, OPEN-LABEL SAFETY AND DOSE-FINDING STUDY OF ADENO-ASSOCIATED VIRUS (AAV) SEROTYPE 8 (AAV8)-MEDIATED GENE TRANSFER OF GLUCOSE-6-PHOSPHATASE (G6PASE) IN ADULTS WITH GLYCOGEN STORAGE DISEASE TYPE IA (GSDIA)

Registry ID

401GSDIA01

Source registry

HEALTH_CANADA

Status

Closed

Phase

PHASE1

Study type

INTERVENTIONAL

Sponsor

ULTRAGENYX PHARMACEUTICAL INC

Start date

2020-12-18

Completion date

2021-03-10

Last update

2018-06-29

Conditions

• GLYCOGEN STORAGE DISEASE TYPE IA

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