A LONG-TERM FOLLOW-UP STUDY TO EVALUATE THE SAFETY AND EFFICACY OF ADENO-ASSOCIATED VIRUS (AAV) SEROTYPE 8 (AAV8)-MEDIATED GENE TRANSFER OF GLUCOSE-6-PHOSPHATASE (G6PASE) IN ADULTS WITH GLYCOGEN STORAGE DISEASE TYPE IA (GSDIA)

Registry ID

401GSDIA02

Source registry

HEALTH_CANADA

Status

Closed

Study type

INTERVENTIONAL

Sponsor

ULTRAGENYX PHARMACEUTICAL INC

Start date

2023-10-25

Completion date

2025-07-08

Last update

2020-06-04

Conditions

• GLYCOGEN STORAGE DISEASE TYPE IA

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