A GLOBAL PHASE 3 OPEN-LABEL EXTENSION STUDY TO ASSESS THE LONG-TERM SAFETY,
TOLERABILITY, AND EFFICACY OF INTRAVENOUS AOC 1001 FOR THE TREATMENT OF
MYOTONIC DYSTROPHY TYPE 1
- Registry ID
- AOC 1001-CS4
- Source registry
- HEALTH_CANADA
- Status
- Ongoing
- Phase
- PHASE3
- Study type
- INTERVENTIONAL
- Sponsor
- AVIDITY BIOSCIENCES
- Start date
- 2026-01-12
- Last update
- 2025-08-28
Conditions
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