AN OPEN-LABEL EXTENSION STUDY EVALUATING SAFETY AND PHARMACOKINETICS IN
PARTICIPANTS WITH MYOTONIC DYSTROPHY TYPE 1 (FREEDOM-OLE)
- Registry ID
- PGN-EDODM1-103
- Source registry
- HEALTH_CANADA
- Status
- Ongoing
- Study type
- INTERVENTIONAL
- Sponsor
- PEPGEN INC.
- Start date
- 2025-12-03
- Last update
- 2025-07-08
Conditions
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