AN ADAPTIVE, OPEN-LABEL, MULTINATIONAL PHASE 1/2 STUDY OF THE SAFETY AND EFFICACY OF EX VIVO, LENTIVIRAL VECTOR-MEDIATED GENE THERAPY AVR-RD-02 FOR SUBJECTS WITH TYPE 1 GAUCHER DISEASE

Registry ID
AVRO-RD-02-201
Source registry
HEALTH_CANADA
Status
Ongoing
Phase
PHASE1
Study type
INTERVENTIONAL
Sponsor
AVROBIO INC
Start date
2021-05-05
Last update
2018-09-28

Conditions

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