A PHASE 3 SAFETY AND EFFICACY TRIAL OF FLT201 GENE THERAPY IN PATIENTS WITH GAUCHER DISEASE TYPE 1

Registry ID
FLT201-03
Source registry
HEALTH_CANADA
Status
Ongoing
Phase
PHASE3
Study type
INTERVENTIONAL
Sponsor
SPUR THERAPEUTICS LIMITED
Start date
2026-04-28
Last update
2025-12-23

Conditions

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