INTERNATIONAL, MULTI-CENTER, DOUBLE BLIND 9-MONTH FOLLOW-UP EXTENSION STUDY ASSESSING THE LONG TERM SAFETY AND TOLERABILITY OF PXT3003 IN PATIENTS WITH CHARCOT-MARIE-TOOTH DISEASE TYPE 1A

Registry ID

CLN-PXT3003-03

Source registry

HEALTH_CANADA

Status

Ongoing

Study type

INTERVENTIONAL

Sponsor

PHARNEXT

Start date

2018-12-14

Last update

2017-07-26

Conditions

• CHARCOT-MARIE-TOOTH DISEASE TYPE 1A

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