PHASE 3B, OPEN-LABEL, MULTICENTER, SINGLE-DOSE STUDY INVESTIGATING EFFICACY AND SAFETY OF CSL222 (ETRANACOGENE DEZAPARVOVEC) GENE THERAPY ADMINISTERED TO ADULT SUBJECTS WITH SEVERE OR MODERATELY SEVERE HEMOPHILIA B WITH DETECTABLE PRETREATMENT AAV5 NEUTRALIZING ANTIBODIES
- Registry ID
- CSL222_3005
- Source registry
- HEALTH_CANADA
- Status
- Ongoing
- Phase
- PHASE3
- Study type
- INTERVENTIONAL
- Sponsor
- CSL BEHRING
- Start date
- 2025-09-09
- Last update
- 2023-08-16
Conditions
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