A TWO-PART OPEN-LABEL STUDY OF REGV131-LNP1265, A CRISPR/CAS9-BASED
COAGULATION FACTOR IX GENE INSERTION THERAPY IN PARTICIPANTS WITH HEMOPHILIA B
- Registry ID
- R131L1265-HEMB-2318
- Source registry
- HEALTH_CANADA
- Status
- Ongoing
- Study type
- INTERVENTIONAL
- Sponsor
- REGENERON PHARMACEUTICALS INC
- Start date
- 2025-03-20
- Last update
- 2024-06-21
Conditions
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