A PHASE 3, RANDOMIZED, DOUBLE-BLIND, PLACEBO-CONTROLLED STUDY OF ADENOASSOCIATED VIRUS SEROTYPE 8-MEDIATED GENE TRANSFER OF GLUCOSE-6- PHOSPHATASE IN PATIENTS WITH GLYCOGEN STORAGE DISEASE TYPE IA

Registry ID

DTX401-CL301

Source registry

HEALTH_CANADA

Status

Closed

Phase

PHASE3

Study type

INTERVENTIONAL

Sponsor

ULTRAGENYX PHARMACEUTICAL INC

Start date

2023-12-18

Completion date

2026-04-21

Last update

2021-10-08

Conditions

• GLYCOGEN STORAGE DISEASE TYPE IA

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