RANDOMIZED, MULTI-CENTER, DOUBLE-BLIND, SHAM-CONTROLLED, PARALLEL GROUP, PHASE III CLINICAL STUDY TO EVALUATE THE EFFICACY AND SAFETY OF INTRATHECALLY ADMINISTERED RUGONERSEN IN PEDIATRIC AND ADULT PARTICIPANTS WITH ANGELMAN SYNDROME

Registry ID

OHB-724-301

Source registry

HEALTH_CANADA

Status

Pending

Phase

PHASE3

Study type

INTERVENTIONAL

Sponsor

OHB PEDIATRICS LTD.

Last update

2026-05-06

Conditions

• ANGELMAN SYNDROME (AS)

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