A LONG-TERM FOLLOW-UP STUDY OF SUBJECTS WITH BETA-THALASSEMIA OR SICKLE CELL DISEASE TREATED WITH AUTOLOGOUS CRISPR-CAS9 MODIFIED HEMATOPOIETIC STEM CELLS (CTX001)
- Registry ID
- VX18-CTX001-131
- Source registry
- HEALTH_CANADA
- Status
- Ongoing
- Study type
- INTERVENTIONAL
- Sponsor
- VERTEX PHARMACEUTICALS INC
- Start date
- 2021-06-04
- Last update
- 2019-03-05
Conditions
- BETA-THALASSEMIA
- SICKLE CELL DISEASE
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