A PHASE 1/2A DOUBLE-BLIND, PLACEBO-CONTROLLED, SINGLE- AND MULTIPLE ASCENDING DOSE STUDY TO ASSESS THE SAFETY, TOLERABILITY, PHARMACOKINETICS, PHARMACODYNAMICS AND PRELIMINARY CLINICAL EFFICACY OF INTRAVENOUS ADMINISTRATION OF ATX-01 IN MALE AND FEMALE PARTICIPANTS AGED 18 TO 64 WITH CLASSIC MYOTONIC DYSTROPHY TYPE 1 (DM1)
- Registry ID
- CT-ATX-01-DM1-1.1
- Source registry
- HEALTH_CANADA
- Status
- Ongoing
- Phase
- PHASE1
- Study type
- INTERVENTIONAL
- Sponsor
- ARTHEX BIOTECH, S.L.
- Start date
- 2026-06-23
- Last update
- 2024-03-14
Conditions
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