A RANDOMIZED, DOUBLE-BLIND, PLACEBO-CONTROLLED STUDY TO EVALUATE THE SAFETY AND EFFICACY OF PITOLISANT ON EXCESSIVE DAYTIME SLEEPINESS AND OTHER NON-MUSCULAR SYMPTOMS IN PATIENTS WITH MYOTONIC DYSTROPHY TYPE 1, FOLLOWED BY AN OPEN-LABEL EXTENSION
- Registry ID
- HBS-101-CL-005
- Source registry
- HEALTH_CANADA
- Status
- Closed
- Study type
- INTERVENTIONAL
- Sponsor
- HARMONY BIOSCIENCES, LLC
- Start date
- 2023-10-03
- Completion date
- 2024-10-31
- Last update
- 2022-01-12
Conditions
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